A | B | C | |
---|---|---|---|
1 | Main | ||
2 | Brand | Onpattro | |
3 | Generic | patisiran | |
4 | Indication | ATTR Amyloidosis. Neuropathy & Cardiomyopathy. | |
5 | Clinical Trials | ||
6 | Phase III "APOLLO-B" n=360 ATTR with cardiomyopathy | ||
7 | 6MW PE met at 12 months: +14.7m, p=0.0162 | ||
8 | '-8.15 for patisiran, -21.345 for placebo | ||
9 | Initially presented at ISA, press release 8/2022; HFSA 10/2022 | ||
10 | 0.3mg/kg IV q3w | ||
11 | MACE HR=0.839 p=NS |